Drug details

Skysona (elivaldogene autotemcel suspension for intravenous infusion)

type of Regenerative Therapy

Skysona (elivaldogene autotemcel) is indicated to slow the progression of neurologic
dysfunction in boys 4-17 years of age with early, active cerebral adrenoleukodystrophy (CALD). Early, active CALD
refers to asymptomatic or mildly symptomatic (neurologic function score, NFS ≤ 1) boys
who have gadolinium enhancement on brain magnetic resonance imaging (MRI) and Loes scores of
0.5-9.

This drug may have the following side effects:
  • hives,
  • difficulty breathing,
  • swelling of your face, lips, tongue, or throat,
  • nausea,
  • rash,
  • vomiting,
  • diarrhea,
  • fever,
  • skin rash,
  • easy bruising,
  • pale skin,
  • shortness of breath,
  • chills,
  • shortness of breath,
  • seizure,
  • constipation,
  • dry mouth,
  • headache,
  • fatigue,
  • sweating,
  • cough,
  • trouble swallowing,
  • vomiting
  • painful urination,
  • increased urination,
  • congestion,
  • abdominal pain,
  • hair loss,
  • fast heartbeat,
  • easy bruising, and
  • red or swollen gums,
  • frequent urination,
  • white patches in your mouth,
  • neck or back pain,
  • decreased appetite,
  • inflammation of mucus membranes,
  • febrile neutropenia,
  • Abnormal bleeding,
  • joint pain and swelling,
  • sores in the mouth,
  • pain when urinating,
  • sores or pain around the anus,
  • unusual vaginal discharge or itching,
  • pain in your ears and discharge,
  • pus filled pimples,
  • pain, redness and swelling of your eyes,
  • pus or discharge from a wound,
  • severe coughing,
  • purple or red spots on the skin,
  • vascular device infection,
  • increased or thicker saliva in the mouth, and
  • paleness
  • low white blood cell count (leukopenia, lymphopenia, neutropenia),
  • low platelets (thrombocytopenia),
  • low iron (anemia), and
  • low potassium (hypokalemia).